@article{article, title = {{Issues, challenges and opportunities for economic evaluations of orphan drugs in rare diseases: an umbrella review}}, publisher = {{Springer Science and Business Media LLC}}, url = {{https://eprints.whiterose.ac.uk/id/eprint/211668 }}, year = {{2024}}, month = {{4}}, author = {{Grand TS and Ren S and Hall J and Åström DO and Regnier S and Thokala P}}, doi = {{10.1007/s40273-024-01370-2}}, volume = {{42}}, journal = {{PharmacoEconomics}}, issue = {{6}}, pages = {{619-631}}, note = {{Accessed on 2025/11/02}}}