TY - JOUR T1 - Issues, challenges and opportunities for economic evaluations of orphan drugs in rare diseases: an umbrella review JO - PharmacoEconomics UR - https://eprints.whiterose.ac.uk/id/eprint/211668 PY - 2024/04/14 AU - Grand TS AU - Ren S AU - Hall J AU - Åström DO AU - Regnier S AU - Thokala P ED - DO - DOI: 10.1007/s40273-024-01370-2 PB - Springer Science and Business Media LLC VL - 42 IS - 6 SP - 619 EP - 631 Y2 - 2025/11/02 ER -