TY - GEN T1 - Issues, challenges and opportunities for economic evaluation of orphan drugs: an umbrella review protocol PY - -0001/11/30 AU - Grand T AU - Ren S AU - Thokala P AU - Åström DO AU - Regnier S AU - Hall J ED - DO - DOI: 10.15131/shef.data.23390060 Y2 - 2026/06/13 ER -