@article{article, title = {{Efficacy and Safety of Asfotase Alfa in Infants and Young Children With Hypophosphatasia: A Phase 2 Open-Label Study}}, publisher = {{Oxford University Press (on behalf of the Endocrine Society)}}, url = {{}}, year = {{2019}}, month = {{7}}, author = {{Hofmann CE and Harmatz P and Vockley J and Högler W and Nakayama H and Bishop N and Martos-Moreno GÁ and Moseley S and Fujita KP and Liese J and Rockman-Greenberg C}}, doi = {{10.1210/jc.2018-02335}}, volume = {{104}}, journal = {{The Journal of Clinical Endocrinology & Metabolism}}, issue = {{7}}, pages = {{2735-2747}}, note = {{Accessed on 2025/11/04}}}