TY - JOUR T1 - Challenges in Gene‐Directed Therapies for Rare Neurodevelopmental Disorders Using HNRNPU as an Exemplar JO - Clinical Genetics UR - https://doi.org/10.1111/cge.70267 PY - 2026/10/22 AU - Aiyedun D AU - Rogers SF AU - Taha DM AU - Balasubramanian M ED - DO - DOI: 10.1111/cge.70267 PB - Wiley Y2 - 2026/10/25 ER -