@article{article, title  = {{Safety, tolerability, and pharmacokinetics of antisense oligonucleotide BIIB078 in adults with C9orf72-associated amyotrophic lateral sclerosis: a phase 1, randomised, double blinded, placebo-controlled, multiple ascending dose study}},

 publisher = {{Elsevier BV}},

 url = {{https://eprints.whiterose.ac.uk/id/eprint/228909 }},

 year = {{2024}},

 month = {{7}},

 author = {{van den Berg LH and Rothstein JD and Shaw PJ and Babu S and Benatar M and Bucelli RC and Genge A and Glass JD and Hardiman O and Libri V and Mobach T et al}},

 doi = {{10.1016/s1474-4422(24)00216-3}},

 volume = {{23}},

 journal = {{The Lancet Neurology}},

 issue = {{9}},

 pages = {{901-912}},

 note = {{Accessed on 2025/11/27}}}