TY  - JOUR

T1  - Safety, tolerability, and pharmacokinetics of antisense oligonucleotide BIIB078 in adults with C9orf72-associated amyotrophic lateral sclerosis: a phase 1, randomised, double blinded, placebo-controlled, multiple ascending dose study

JO  - The Lancet Neurology

UR  - https://eprints.whiterose.ac.uk/id/eprint/228909

PY  - 2024/07/23

AU  - van den Berg LH

AU  - Rothstein JD

AU  - Shaw PJ

AU  - Babu S

AU  - Benatar M

AU  - Bucelli RC

AU  - Genge A

AU  - Glass JD

AU  - Hardiman O

AU  - Libri V

AU  - Mobach T et al

ED  - 

DO  - DOI: 10.1016/s1474-4422(24)00216-3

PB  - Elsevier BV

VL  - 23

IS  - 9

SP  - 901

EP  - 912

Y2  - 2025/11/27

ER  -